Gene Therapy in Ophthalmology: Advances and Challenges  

Gene therapy has emerged as a promising frontier in 
modern medicine, offering potential cures for previously 
untreatable genetic disorders. These therapies target the 
rarest of diseases, collectively afflicting millions of people 
worldwide, where a genetic defect modifies or prevents 
the proper functioning of cells, often leading to 
life-threatening conditions. 

In this whitepaper, we'll look at in vivo and ex vivo approaches and dive into the devices, challenges and delivery method.